Satya
Bio
Targets
Companies
Extract
Insights
About
Get Started
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Companies
Biotech and pharma companies with clinical data analysis
181
Companies
7
With Data
17
High Priority
Stage
All
Company maturity based on pipeline and revenue stage
[{'id': 'large_cap_diversified', 'name': 'Large Cap Diversified', 'description': 'Multiple approved products, diversified pipeline, typically >$10B market cap', 'examples': ['ABBV', 'BMY', 'GILD']}, {'id': 'commercial_stage', 'name': 'Commercial Stage', 'description': '1-3 approved products generating revenue, active pipeline', 'examples': ['ARGX', 'BMRN', 'ALNY']}, {'id': 'late_clinical', 'name': 'Late Clinical', 'description': 'Lead asset in Phase 3 or NDA/BLA filed, pre-revenue or minimal revenue', 'examples': ['NUVL', 'ASND', 'KRYS']}, {'id': 'mid_clinical', 'name': 'Mid Clinical', 'description': 'Lead asset in Phase 2, proof-of-concept data available or pending', 'examples': ['KYMR', 'EWTX', 'CNTA']}, {'id': 'early_clinical', 'name': 'Early Clinical', 'description': 'Lead asset in Phase 1 or IND-enabling, high-risk/high-reward', 'examples': ['SLNO', 'ADMA']}]
Modality
All
Primary therapeutic modality/platform technology
[{'id': 'small_molecule', 'name': 'Small Molecule', 'description': 'Traditional oral/injectable small molecule drugs', 'subtypes': ['Kinase Inhibitor', 'Degrader/PROTAC', 'Molecular Glue', 'Enzyme Inhibitor', 'GPCR Modulator']}, {'id': 'antibody_biologics', 'name': 'Antibody/Biologics', 'description': 'Monoclonal antibodies, bispecifics, ADCs, fusion proteins', 'subtypes': ['mAb', 'Bispecific', 'ADC', 'Fc-Fusion', 'Nanobody']}, {'id': 'rna_therapeutics', 'name': 'RNA Therapeutics', 'description': 'mRNA, siRNA, ASO-based therapeutics', 'subtypes': ['mRNA', 'siRNA', 'ASO', 'saRNA']}, {'id': 'gene_therapy', 'name': 'Gene Therapy', 'description': 'AAV, lentiviral, and other gene delivery platforms', 'subtypes': ['AAV', 'Lentiviral', 'Non-Viral', 'Gene Editing']}, {'id': 'cell_therapy', 'name': 'Cell Therapy', 'description': 'CAR-T, CAR-NK, TIL, and other cell-based therapies', 'subtypes': ['CAR-T', 'CAR-NK', 'TIL', 'Stem Cell', 'iPSC-derived']}, {'id': 'oligonucleotide', 'name': 'Oligonucleotide', 'description': 'Antisense, splice-switching, and other oligo-based approaches', 'subtypes': ['Splice Modulator', 'Exon Skipping', 'Gene Silencing']}]
Therapeutic Area
All
Primary therapeutic focus area
[{'id': 'oncology_precision', 'name': 'Oncology-Precision', 'description': 'Targeted oncology with biomarker-driven patient selection', 'subtypes': ['Solid Tumor', 'Hematologic', 'Rare Cancer']}, {'id': 'oncology_io', 'name': 'Oncology-IO', 'description': 'Immuno-oncology approaches (checkpoint, cell therapy, etc.)', 'subtypes': ['Checkpoint', 'Cell Therapy', 'Bispecific', 'ADC']}, {'id': 'rare_genetic', 'name': 'Rare-Genetic', 'description': 'Rare diseases with clear genetic etiology', 'subtypes': ['Neurologic', 'Metabolic', 'Hematologic', 'Muscular']}, {'id': 'rare_metabolic', 'name': 'Rare-Metabolic', 'description': 'Rare metabolic disorders and enzyme deficiencies', 'subtypes': ['Lysosomal Storage', 'Amino Acid', 'Lipid']}, {'id': 'neuropsychiatry', 'name': 'Neuropsychiatry', 'description': 'CNS disorders including neuro and psychiatric conditions', 'subtypes': ['Neurodegenerative', 'Psychiatric', 'Pain', 'Movement Disorder']}, {'id': 'i_and_i_autoimmune', 'name': 'I&I/Autoimmune', 'description': 'Immunology and autoimmune/inflammatory diseases', 'subtypes': ['Dermatology', 'Rheumatology', 'GI', 'Respiratory']}, {'id': 'cardiometabolic', 'name': 'Cardiometabolic', 'description': 'Cardiovascular and metabolic diseases', 'subtypes': ['CV', 'Obesity', 'Diabetes', 'NASH/MASH']}, {'id': 'ophthalmology', 'name': 'Ophthalmology', 'description': 'Eye diseases and vision disorders', 'subtypes': ['Retinal', 'Glaucoma', 'Corneal', 'Dry Eye']}, {'id': 'infectious_disease', 'name': 'Infectious Disease', 'description': 'Vaccines, antivirals, antibiotics', 'subtypes': ['Viral', 'Bacterial', 'Vaccines']}]
Thesis Type
All
Investment thesis archetype for position sizing and risk management
[{'id': 'platform_royalty', 'name': 'Platform/Royalty', 'description': 'Value driven by platform partnerships, royalties, or multiple pipeline shots on goal', 'characteristics': ['Diversified risk', 'Recurring revenue potential', 'Partner validation'], 'examples': ['ROIV', 'ALNY']}, {'id': 'binary_event', 'name': 'Binary Event', 'description': 'Near-term catalyst (data readout, approval) that will significantly move stock', 'characteristics': ['High conviction required', 'Position sizing critical', 'Defined timeline'], 'examples': ['ASND', 'NUVL']}, {'id': 'commercial_compounder', 'name': 'Commercial Compounder', 'description': 'Growing commercial franchise with predictable revenue trajectory', 'characteristics': ['Revenue visibility', 'Execution focus', 'Multiple expansion potential'], 'examples': ['ARGX', 'INSM']}, {'id': 'sum_of_parts', 'name': 'Sum-of-Parts', 'description': 'Multiple undervalued assets where total value > current market cap', 'characteristics': ['Catalyst-rich', 'Option value', 'Potential for re-rating'], 'examples': ['KYMR', 'ARDX']}, {'id': 'ma_target', 'name': 'M&A Target', 'description': 'Strategic asset likely to be acquired, floor valuation from takeout', 'characteristics': ['Strategic fit', 'Scarcity value', 'Clean structure'], 'examples': ['SLNO', 'HALO']}]
Priority
All
High
Medium
Low
Data Status
All
Has Data
No Data
Apply Filters
Clear
ARGX
Mid Clinical
Has Data
argenx SE
Mixed
·
Mixed
ARWR
Platform
Has Data
Arrowhead Pharmaceuticals
Rna Therapeutics
·
Mixed
RNAi platform with extra-hepatic delivery (TRiM). 1 approved (REDEMPLO), 3 Phase 3
ASND
Mid Clinical
Has Data
Ascendis Pharma
Mixed
·
Mixed
CDTX
Mid Clinical
No Data
Cidara Therapeutics
Mixed
·
Mixed
CNTA
Mid Clinical
No Data
Centessa Pharmaceuticals
Mixed
·
Mixed
ELVN
Mid Clinical
No Data
Enliven Therapeutics
Mixed
·
Mixed
EWTX
Mid Clinical
Has Data
Edgewise Therapeutics
Mixed
·
Mixed
GPCR
Mid Clinical
No Data
Structure Therapeutics
Mixed
·
Mixed
KYMR
Mid Clinical
Has Data
Kymera Therapeutics
Mixed
·
Mixed
MLYS
Mid Clinical
No Data
Mineralys Therapeutics
Mixed
·
Mixed
NAMS
Mid Clinical
No Data
NewAmsterdam Pharma
Mixed
·
Mixed
NUVL
Mid Clinical
Has Data
Nuvalent
Mixed
·
Mixed
OCUL
Mid Clinical
No Data
Ocular Therapeutix
Mixed
·
Mixed
ORKA
Mid Clinical
No Data
Oruka Therapeutics
Mixed
·
Mixed
SION
Mid Clinical
No Data
Sionna Therapeutics
Mixed
·
Mixed
SLNO
Mid Clinical
No Data
Soleno Therapeutics
Mixed
·
Mixed
TRML
Mid Clinical
No Data
Tourmaline Bio
Mixed
·
Mixed
ACRV
Mid Clinical
No Data
Acrivon Therapeutics
Mixed
·
Mixed
ALNY
Platform
No Data
Alnylam Pharmaceuticals
Mixed
·
Mixed
RNA therapeutics leader
ARTV
Mid Clinical
No Data
Artiva Biotherapeutics
Mixed
·
Mixed
BCAX
Mid Clinical
No Data
Bicara Therapeutics
Mixed
·
Mixed
CLYM
Mid Clinical
No Data
Climb Bio
Mixed
·
Mixed
CTMX
Mid Clinical
No Data
CytomX Therapeutics
Mixed
·
Mixed
DNTH
Mid Clinical
No Data
Dianthus Therapeutics
Mixed
·
Mixed
ELDN
Mid Clinical
No Data
Eledon Pharmaceuticals
Mixed
·
Mixed
FDMT
Mid Clinical
No Data
4D Molecular Therapeutics
Mixed
·
Mixed
GHRS
Mid Clinical
No Data
GH Research
Mixed
·
Mixed
GKOS
Mid Clinical
No Data
Glaukos
Mixed
·
Mixed
HOWL
Mid Clinical
No Data
Werewolf Therapeutics
Mixed
·
Mixed
INSP
Mid Clinical
No Data
Inspire Medical Systems
Mixed
·
Mixed
IRON
Mid Clinical
No Data
Disc Medicine
Mixed
·
Mixed
JBIO
Mid Clinical
No Data
Jade Biosciences
Mixed
·
Mixed
LENZ
Mid Clinical
No Data
Lenz Therapeutics
Mixed
·
Mixed
LRMR
Mid Clinical
No Data
Larimar Therapeutics
Mixed
·
Mixed
MTSR
Mid Clinical
No Data
Metsera
Mixed
·
Mixed
NKTX
Mid Clinical
No Data
Nkarta
Mixed
·
Mixed
PEPG
Mid Clinical
No Data
PepGen
Mixed
·
Mixed
PHVS
Mid Clinical
No Data
Pharvaris
Mixed
·
Mixed
SEPN
Mid Clinical
No Data
Septerna
Mixed
·
Mixed
SLDB
Mid Clinical
No Data
Solid Biosciences
Mixed
·
Mixed
SPRY
Mid Clinical
No Data
ARS Pharmaceuticals
Mixed
·
Mixed
SRZN
Mid Clinical
No Data
Surrozen
Mixed
·
Mixed
TNGX
Mid Clinical
No Data
Tango Therapeutics
Mixed
·
Mixed
TSHA
Mid Clinical
No Data
Taysha Gene Therapies
Mixed
·
Mixed
TYRA
Mid Clinical
No Data
Tyra Biosciences
Mixed
·
Mixed
WGS
Mid Clinical
No Data
GeneDx
Mixed
·
Mixed
ABBV
Mid Clinical
No Data
AbbVie
Mixed
·
Mixed
I&I, Oncology, Neuro. Key products: Humira, Skyrizi, Rinvoq.
ABUS
Mid Clinical
No Data
Arbutus Biopharma
Mixed
·
Mixed
Infectious - HBV cure.
ACAD
Mid Clinical
No Data
Acadia Pharmaceuticals
Mixed
·
Mixed
Neuropsychiatry. Key products: Nuplazid, Daybue.
ACLX
Mid Clinical
No Data
Arcellx
Mixed
·
Mixed
Oncology - CAR-T.
ADMA
Mid Clinical
No Data
ADMA Biologics
Mixed
·
Mixed
I&I (Immunoglobulins). Key product: ASCENIV.
AGIO
Mid Clinical
No Data
Agios Pharmaceuticals
Mixed
·
Mixed
Rare - Hematology. Key product: Pyrukynd.
AKBA
Mid Clinical
No Data
Akebia Therapeutics
Mixed
·
Mixed
Nephrology - anemia.
AKRO
Mid Clinical
No Data
Akero Therapeutics
Mixed
·
Mixed
Metabolic - MASH. Lead: efruxifermin.
ALEC
Mid Clinical
No Data
Alector
Mixed
·
Mixed
Neurodegeneration - immuno-neurology.
ALKS
Mid Clinical
No Data
Alkermes
Mixed
·
Mixed
Neuropsychiatry. Key products: Vivitrol, Aristada.
ALT
Mid Clinical
No Data
Altimmune
Mixed
·
Mixed
Metabolic - obesity.
AMGN
Mid Clinical
No Data
Amgen
Mixed
·
Mixed
Oncology, I&I, Bone. Key products: Repatha, Prolia, Lumakras.
ANAB
Mid Clinical
No Data
AnaptysBio
Mixed
·
Mixed
I&I - Dermatology. Lead: rosnilimab.
ANNX
Mid Clinical
No Data
Annexon Biosciences
Mixed
·
Mixed
Neuro - complement C1q.
APGE
Mid Clinical
No Data
Apogee Therapeutics
Mixed
·
Mixed
I&I - next-gen biologics.
APLS
Mid Clinical
No Data
Apellis Pharmaceuticals
Mixed
·
Mixed
Ophthalmology. Key product: Syfovre.
ARDX
Commercial Stage
Has Data
Ardelyx
Small Molecule
·
Gi Nephrology
Commercial-stage GI/nephrology. IBSRELA (IBS-C, 92% YoY growth), XPHOZAH (hyperphosphatemia). NHE3 platform.
ARVN
Mid Clinical
No Data
Arvinas
Mixed
·
Mixed
Oncology - protein degraders.
AXSM
Mid Clinical
No Data
Axsome Therapeutics
Mixed
·
Mixed
Neuropsychiatry. Key products: Auvelity, Sunosi.
BCRX
Mid Clinical
No Data
BioCryst Pharmaceuticals
Mixed
·
Mixed
Rare Disease. Key product: Orladeyo.
BEAM
Platform
No Data
Beam Therapeutics
Mixed
·
Mixed
Rare Disease (Gene Editing). Lead: BEAM-101 (Ph1/2).
BHVN
Mid Clinical
No Data
Biohaven
Mixed
·
Mixed
Neuropsychiatry. Lead: taldefgrobep.
BIIB
Mid Clinical
No Data
Biogen
Mixed
·
Mixed
Neuropsychiatry. Key products: Leqembi, Spinraza, Tysabri.
BLUE
Platform
No Data
bluebird bio
Mixed
·
Mixed
Gene Therapy. Key products: Zynteglo, Lyfgenia.
BMRN
Mid Clinical
No Data
BioMarin Pharmaceutical
Mixed
·
Mixed
Rare Disease. Key products: Voxzogo, Palynziq, Roctavian.
BNTX
Mid Clinical
No Data
BioNTech
Mixed
·
Mixed
mRNA vaccines and oncology.
CALT
Mid Clinical
No Data
Calliditas Therapeutics
Mixed
·
Mixed
Rare - IgAN. Key product: Tarpeyo.
CBAY
Mid Clinical
No Data
CymaBay Therapeutics
Mixed
·
Mixed
Metabolic - PBC. Key product: seladelpar.
CDNA
Mid Clinical
No Data
CareDx
Mixed
·
Mixed
Dx - Transplant. Key product: AlloSure.
COGT
Mid Clinical
No Data
Cogent Biosciences
Mixed
·
Mixed
Oncology - KIT inhibitor.
CPRX
Mid Clinical
No Data
Catalyst Pharmaceuticals
Mixed
·
Mixed
Neuropsychiatry. Key product: Firdapse.
CRNX
Mid Clinical
No Data
Crinetics Pharmaceuticals
Mixed
·
Mixed
Endocrinology. Lead: paltusotine.
CRSP
Platform
No Data
CRISPR Therapeutics
Mixed
·
Mixed
Rare Disease (Gene Editing). Key product: Casgevy.
CYTK
Mid Clinical
No Data
Cytokinetics
Mixed
·
Mixed
Cardiovascular. Key product: Myqorzo.
DAWN
Mid Clinical
No Data
Day One Biopharmaceuticals
Mixed
·
Mixed
Oncology - pediatric. Key product: Ojemda.
DNLI
Commercial Stage
No Data
Denali Therapeutics
Mixed
·
Mixed
Neurodegeneration. Lead: DNL310.
DVAX
Mid Clinical
No Data
Dynavax Technologies
Mixed
·
Mixed
Vaccines. Key product: Heplisav-B.
DYN
Platform
No Data
Dyne Therapeutics
Mixed
·
Mixed
Neuromuscular - AOC platform.
EDIT
Platform
No Data
Editas Medicine
Mixed
·
Mixed
Gene Editing - in vivo.
ETNB
Mid Clinical
No Data
89bio
Mixed
·
Mixed
Metabolic - MASH. Lead: pegozafermin.
EXAS
Mid Clinical
No Data
Exact Sciences
Mixed
·
Mixed
Dx - Oncology. Key products: Cologuard, Oncotype DX.
EXEL
Mid Clinical
No Data
Exelixis
Mixed
·
Mixed
Oncology. Key product: Cabometyx.
FATE
Platform
No Data
Fate Therapeutics
Mixed
·
Mixed
iPSC-derived cell therapy.
FGEN
Mid Clinical
No Data
FibroGen
Mixed
·
Mixed
Fibrosis, Anemia. Lead: pamrevlumab.
FOLD
Mid Clinical
No Data
Amicus Therapeutics
Mixed
·
Mixed
Rare - Lysosomal. Key products: Galafold, Pombiliti.
FULC
Mid Clinical
No Data
Fulcrum Therapeutics
Mixed
·
Mixed
Rare Disease. Lead: losmapimod.
GERN
Mid Clinical
No Data
Geron Corporation
Mixed
·
Mixed
Oncology - telomerase. Key product: Rytelo.
GH
Mid Clinical
No Data
Guardant Health
Mixed
·
Mixed
Dx - Oncology. Key products: Guardant360, Shield.
GILD
Mid Clinical
No Data
Gilead Sciences
Mixed
·
Mixed
HIV, Oncology, Liver. Key products: Biktarvy, Trodelvy, Livdelzi.
GRAL
Mid Clinical
No Data
Grail
Mixed
·
Mixed
Dx - Oncology. Key product: Galleri.
HALO
Platform
No Data
Halozyme Therapeutics
Mixed
·
Mixed
Drug Delivery. ENHANZE royalties.
HIMS
Mid Clinical
No Data
Hims & Hers Health
Mixed
·
Mixed
Telehealth - consumer health.
IDYA
Mid Clinical
No Data
IDEAYA Biosciences
Mixed
·
Mixed
Oncology - synthetic lethality.
IGMS
Mid Clinical
No Data
IGM Biosciences
Mixed
·
Mixed
Oncology - IgM antibodies.
IMGN
Mid Clinical
No Data
ImmunoGen
Mixed
·
Mixed
Oncology - ADC. Key product: Elahere.
IMTX
Mid Clinical
No Data
Immatics
Mixed
·
Mixed
Oncology - TCR-T.
IMVT
Mid Clinical
No Data
Immunovant
Mixed
·
Mixed
I&I (FcRn). Lead: batoclimab (Ph3).
INCY
Mid Clinical
No Data
Incyte
Mixed
·
Mixed
Oncology, I&I. Key products: Jakafi, Opzelura.
INSM
Mid Clinical
No Data
Insmed
Mixed
·
Mixed
Rare - Pulmonary. Key products: Arikayce, Brinsupri.
IONS
Platform
No Data
Ionis Pharmaceuticals
Mixed
·
Mixed
Neuro, Cardio, Rare. Key products: SPINRAZA, WAINUA.
IOVA
Mid Clinical
No Data
Iovance Biotherapeutics
Mixed
·
Mixed
Oncology - TIL therapy. Key product: Amtagvi.
IRWD
Mid Clinical
No Data
Ironwood Pharmaceuticals
Mixed
·
Mixed
GI. Key product: Linzess.
ITCI
Mid Clinical
No Data
Intra-Cellular Therapies
Mixed
·
Mixed
Neuropsychiatry. Key product: Caplyta.
JANX
Mid Clinical
No Data
Janux Therapeutics
Mixed
·
Mixed
Oncology - T cell engagers. Lead: JANX007.
KALA
Mid Clinical
No Data
Kala Pharmaceuticals
Mixed
·
Mixed
Ophthalmology. Key product: Eysuvis.
KALV
Mid Clinical
No Data
KalVista Pharmaceuticals
Mixed
·
Mixed
Rare - HAE. Lead: sebetralstat.
KROS
Mid Clinical
No Data
Keros Therapeutics
Mixed
·
Mixed
Hematology. Lead: elritercept.
KRYS
Platform
No Data
Krystal Biotech
Mixed
·
Mixed
Rare - Dermatology. Key product: Vyjuvek.
LEGN
Commercial Stage
No Data
Legend Biotech
Mixed
·
Mixed
Oncology - CAR-T. Key product: Carvykti.
LNTH
Mid Clinical
No Data
Lantheus Holdings
Mixed
·
Mixed
Diagnostics - radiopharmaceuticals.
LQDA
Mid Clinical
No Data
Liquidia Technologies
Mixed
·
Mixed
Rare - PAH. Key product: Yutrepia.
LYEL
Mid Clinical
No Data
Lyell Immunopharma
Mixed
·
Mixed
Oncology - next-gen T cell.
MDGL
Mid Clinical
No Data
Madrigal Pharmaceuticals
Mixed
·
Mixed
Metabolic - MASH. Key product: Rezdiffra.
MDXH
Mid Clinical
No Data
MDxHealth
Mixed
·
Mixed
Dx - Urology.
MIRM
Mid Clinical
No Data
Mirum Pharmaceuticals
Mixed
·
Mixed
Rare - Liver. Key product: Livmarli.
MNKD
Commercial Stage
No Data
MannKind
Mixed
·
Mixed
Diabetes, Pulmonary. Key products: Afrezza, Tyvaso DPI.
MRNA
Platform
No Data
Moderna
Mixed
·
Mixed
Vaccines, Oncology, Rare. COVID/RSV vaccines platform.
MRUS
Commercial Stage
No Data
Merus
Mixed
·
Mixed
Oncology - bispecific antibodies. Lead: zenocutuzumab.
MRVI
Mid Clinical
No Data
Maravai LifeSciences
Mixed
·
Mixed
Tools - nucleic acid production.
MYGN
Mid Clinical
No Data
Myriad Genetics
Mixed
·
Mixed
Dx - Oncology, Women's Health.
NBIX
Mid Clinical
No Data
Neurocrine Biosciences
Mixed
·
Mixed
Neuropsychiatry. Key product: Ingrezza.
NTLA
Platform
No Data
Intellia Therapeutics
Mixed
·
Mixed
Rare Disease (Gene Editing). Lead: NTLA-2001 (Ph3).
NTRA
Mid Clinical
No Data
Natera
Mixed
·
Mixed
Dx - Oncology, Prenatal. Key products: Signatera, Panorama.
NUVB
Mid Clinical
No Data
Nuvation Bio
Mixed
·
Mixed
Oncology - targeted therapies.
NVAX
Mid Clinical
No Data
Novavax
Mixed
·
Mixed
Vaccines. COVID vaccine.
OGN
Commercial Stage
No Data
Organon
Mixed
·
Mixed
Women's Health, Biosimilars.
OMER
Mid Clinical
No Data
Omeros Corporation
Mixed
·
Mixed
Complement. Lead: narsoplimab.
PCRX
Commercial Stage
No Data
Pacira BioSciences
Mixed
·
Mixed
Pain management. Key product: Exparel.
PCVX
Mid Clinical
No Data
Vaxcyte
Mixed
·
Mixed
Vaccines - Pneumococcal. Lead: VAX-31.
PRAX
Mid Clinical
No Data
Praxis Precision Medicines
Mixed
·
Mixed
Neuropsychiatry - Genetic CNS.
PRME
Platform
No Data
Prime Medicine
Mixed
·
Mixed
Prime Editing platform. Lead: PM359 (Ph1).
PTCT
Mid Clinical
No Data
PTC Therapeutics
Mixed
·
Mixed
Rare Disease. Key products: Translarna, Evrysdi royalties.
PTGX
Mid Clinical
No Data
Protagonist Therapeutics
Mixed
·
Mixed
GI, Hematology. Lead: rusfertide.
QURE
Platform
No Data
uniQure
Mixed
·
Mixed
Gene Therapy. Key product: Hemgenix.
RARE
Mid Clinical
No Data
Ultragenyx Pharmaceutical
Mixed
·
Mixed
Rare Disease. Key products: Crysvita, Evkeeza.
RCKT
Commercial Stage
No Data
Rocket Pharmaceuticals
Mixed
·
Mixed
Gene Therapy. Key product: Kresladi.
RCUS
Mid Clinical
No Data
Arcus Biosciences
Mixed
·
Mixed
Oncology - immuno-oncology.
REGN
Mid Clinical
No Data
Regeneron Pharmaceuticals
Mixed
·
Mixed
Reference company for Dupixent comparisons
REPL
Mid Clinical
No Data
Replimune Group
Mixed
·
Mixed
Oncology - oncolytic immunotherapy.
RGNX
Platform
No Data
Regenxbio
Mixed
·
Mixed
AAV gene therapy platform. Multiple programs.
RLAY
Mid Clinical
No Data
Relay Therapeutics
Mixed
·
Mixed
Oncology - precision medicine. Lead: RLY-2608.
RNA
Platform
No Data
Avidity Biosciences
Mixed
·
Mixed
Neuromuscular, Cardio. Lead: del-desiran (Ph3).
ROIV
Commercial Stage
No Data
Roivant Sciences
Mixed
·
Mixed
Diversified biotech. Multiple Vants.
RVMD
Commercial Stage
No Data
Revolution Medicines
Mixed
·
Mixed
Oncology - RAS inhibitors. Lead: RMC-6236.
RXRX
Mid Clinical
No Data
Recursion Pharmaceuticals
Mixed
·
Mixed
AI-driven drug discovery.
RYTM
Mid Clinical
No Data
Rhythm Pharmaceuticals
Mixed
·
Mixed
Metabolic - Obesity. Key product: Imcivree.
SAGE
Mid Clinical
No Data
Sage Therapeutics
Mixed
·
Mixed
Neuropsychiatry. Key product: Zurzuvae.
SANA
Platform
No Data
Sana Biotechnology
Mixed
·
Mixed
Cell Engineering platform for hypoimmune cells.
SGMO
Platform
No Data
Sangamo Therapeutics
Mixed
·
Mixed
Gene Therapy, Gene Editing.
SMMT
Commercial Stage
No Data
Summit Therapeutics
Mixed
·
Mixed
Oncology - PD-1. Lead: ivonescimab.
SRPT
Mid Clinical
No Data
Sarepta Therapeutics
Mixed
·
Mixed
Neuromuscular (DMD). Key product: Elevidys.
SRRK
Mid Clinical
No Data
Scholar Rock Holding
Mixed
·
Mixed
Neuromuscular. Lead: apitegromab.
STOK
Mid Clinical
No Data
Stoke Therapeutics
Mixed
·
Mixed
Rare - genetic epilepsies.
SUPN
Commercial Stage
No Data
Supernus Pharmaceuticals
Mixed
·
Mixed
Neuropsychiatry. Key products: Qelbree, Trokendi XR.
TALK
Mid Clinical
No Data
Talkspace
Mixed
·
Mixed
Mental Health - Digital therapeutics.
TARS
Mid Clinical
No Data
Tarsus Pharmaceuticals
Mixed
·
Mixed
Ophthalmology. Key product: Xdemvy.
TCRT
Mid Clinical
No Data
Alaunos Therapeutics
Mixed
·
Mixed
Oncology - TCR-T cell therapy.
TERN
Mid Clinical
No Data
Terns Pharmaceuticals
Mixed
·
Mixed
Metabolic - MASH. Lead: TERN-501.
TGTX
Mid Clinical
No Data
TG Therapeutics
Mixed
·
Mixed
I&I (MS). Key product: Briumvi.
TVTX
Mid Clinical
No Data
Travere Therapeutics
Mixed
·
Mixed
Rare - Nephrology. Key product: Filspari.
TWST
Mid Clinical
No Data
Twist Bioscience
Mixed
·
Mixed
Tools - DNA synthesis platform.
UTHR
Mid Clinical
No Data
United Therapeutics
Mixed
·
Mixed
Rare - PAH. Key product: Tyvaso DPI.
VCEL
Commercial Stage
No Data
Vericel
Mixed
·
Mixed
Regenerative. Key products: MACI, Epicel.
VCYT
Mid Clinical
No Data
Veracyte
Mixed
·
Mixed
Dx - Oncology. Key products: Decipher, Afirma.
VERA
Mid Clinical
No Data
Vera Therapeutics
Mixed
·
Mixed
Nephrology - IgAN. Lead: atacicept.
VERV
Platform
No Data
Verve Therapeutics
Mixed
·
Mixed
Cardiovascular - gene editing.
VIR
Mid Clinical
No Data
Vir Biotechnology
Mixed
·
Mixed
Infectious Disease. Key product: Xofluza partnership.
VKTX
Mid Clinical
No Data
Viking Therapeutics
Mixed
·
Mixed
Metabolic - Obesity/MASH. Lead: VK2735.
VRTX
Mid Clinical
No Data
Vertex Pharmaceuticals
Mixed
·
Mixed
Reference company for CF comparisons
VXRT
Mid Clinical
No Data
Vaxart
Mixed
·
Mixed
Oral vaccines platform.
WVE
Platform
No Data
Wave Life Sciences
Mixed
·
Mixed
Genetic medicines - stereopure.
XENE
Mid Clinical
No Data
Xenon Pharmaceuticals
Mixed
·
Mixed
Neuropsychiatry - Epilepsy. Lead: azetukalner.
XNCR
Mid Clinical
No Data
Xencor
Mixed
·
Mixed
Oncology - bispecific antibodies.
YMAB
Mid Clinical
No Data
Y-mAbs Therapeutics
Mixed
·
Mixed
Oncology - pediatric. Key product: Danyelza.
ZLAB
Commercial Stage
No Data
Zai Lab
Mixed
·
Mixed
China-focused biotech.